PMID: 42415111

Elamipretide in pediatric Barth syndrome: from heart failure to school return.

Amedro Pascal, Andrianoely Mathieu, Gohier Pauline, Leroux Justine, Aladjidi Nathalie, Lagorce Stephanie, Daccord Melissa, Audie Marion, Botte Astrid, Nubret Karine

Orphanet journal of rare diseases · 2026

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This entry links to third-party literature. For research use only.

For research use only. This index links to third-party literature. Nothing here constitutes medical advice.