PMID: 41442049
New advances in treating late-onset Pompe Disease: A narrative review.
Khan Misha, Awan Zainab, Ali Eesha Asghar, Ibrahim Mufliha, Riaz Farhana, Zulfiqar Eeshal, Kumar Ajay, Khan Tariq Mahmood, Amer Samar A
European journal of pediatrics · 2025
Vol. 185, Issue 1, pp. 41
This entry links to third-party literature. For research use only.
HumansGlycogen Storage Disease Type IIEnzyme Replacement TherapyGenetic Therapyalpha-Glucosidases